Updates

June 1, 2020June 1, 2020
Medications to Avoid When You Have LEMS

Lambert-Eaton myasthenic syndrome (LEMS) is a rare autoimmune disease that primarily affects nerve cells and muscles. The immune system mistakenly attacks a specific component ... Read more
May 29, 2020May 29, 2020
COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say

While the ongoing COVID-19 pandemic won’t have much of an impact on cash available for new biotech startups, it has begun to cause delays ... Read more
May 28, 2020May 30, 2020
LEMS-associated Respiratory Problems May Lead to Heart Dysfunction, Case Report Shows

Lambert‐Eaton myasthenic syndrome-associated diaphragm weakness and subsequent respiratory problems may impair heart function, a case study shows. The report, “Lambert Eaton Myasthenic Syndrome Presenting ... Read more
May 27, 2020May 21, 2020
LEMme Tell Ya About Medical Cannabis for Pain Relief

First in a two-part series. I am certain my children never thought they would see the day their mother would use cannabis, let alone ... Read more
May 25, 2020May 25, 2020
Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe

European authorities must step up efforts to screen babies for a multitude of genetic disorders, a panel of experts suggested during a May 14-15 ... Read more

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June 4, 2018June 4, 2018

FDA Accepts Catalyst’s NDA for Firdapse with Priority Review Status for LEMS

News

The U.S. Food and Drug Administration has accepted Catalyst Pharmaceuticals’ new drug application (NDA) for Firdapse (amifampridine phosphate) for Lambert-Eaton myasthenic syndrome (LEMS), with priority review status. Firdapse is a formulation of amifampridine phosphate in development for the treatment of LEMS as ... Read more

Updates

Medications to Avoid When You Have LEMS

COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say

LEMS-associated Respiratory Problems May Lead to Heart Dysfunction, Case Report Shows

LEMme Tell Ya About Medical Cannabis for Pain Relief

Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe

Unity and EU-wide Efforts Focus of Online Rare Disease Meeting

Unity and EU-wide Efforts Focus of Online Rare Disease Meeting

Catalyst Still Expecting Firdapse Approval in Canada in 2020

Why Should I Be Tested for Cancer if Diagnosed with LEMS?

‘LEMme Tell Ya’ Patient Stories in Their Mothers’ Words: Lori Dunham

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Rare Diseases Clinical Research Network Opens Online Survey on COVID-19

Good Long-term Outcomes Seen in Japanese Study, Regardless of Cancer

Honoring Motherless Daughters and Those Who Raised Us

Pregnancy and LEMS

Lower Electromyography Threshold Improves Accuracy of LEMS Diagnosis, Study Suggests

NORD Webinar Outlines COVID-19 Response on Financial, Policy Fronts

Recovery Is a Long Road Following My Concussion

Surge in Telemedicine One ‘Good’ Outcome from COVID-19 Crisis, Doctors Say

Industry leaders seek to advance innovative resources for rare and orphan disease communities amid COVID-19 outbreak

NORD Opens COVID-19 Financial Aid Program for Rare Disease Community

A Cautionary Tale About Hydroxychloroquine’s Side Effects

Catalyst Pharmaceuticals Confirms Sufficient Supply of Firdapse

LEMS and Exercise

The Importance of Being Mindful During COVID-19

Experts Publish Guidance on Managing MG and LEMS During COVID-19 Pandemic

How to Stay Motivated With a Chronic Disease Like LEMS

Mindfulness for People with LEMS

Catalyst Expects No Supply Problems for Firdapse Due to COVID-19

NORD’s Advice on COVID-19: You’re Stronger Than You Think

NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum

Building Emotional Resilience When You Have LEMS

Timely Treatment Can Be Successful for LEMS Linked to Lung Adenocarcinoma, Case Study Suggests

FDA Accepts Catalyst’s NDA for Firdapse with Priority Review Status for LEMS

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Medications to Avoid When You Have LEMS

COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say

LEMS-associated Respiratory Problems May Lead to Heart Dysfunction, Case Report Shows

LEMme Tell Ya About Medical Cannabis for Pain Relief

Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe

Video Games Connect Chronically Ill Children Isolated at Home, Hospital

Unity and EU-wide Efforts Focus of Online Rare Disease Meeting

Unity and EU-wide Efforts Focus of Online Rare Disease Meeting

Catalyst Still Expecting Firdapse Approval in Canada in 2020

Why Should I Be Tested for Cancer if Diagnosed with LEMS?

‘LEMme Tell Ya’ Patient Stories in Their Mothers’ Words: Lori Dunham

Subscribe to our mailing list

Rare Diseases Clinical Research Network Opens Online Survey on COVID-19

Good Long-term Outcomes Seen in Japanese Study, Regardless of Cancer

Honoring Motherless Daughters and Those Who Raised Us

Pregnancy and LEMS

Lower Electromyography Threshold Improves Accuracy of LEMS Diagnosis, Study Suggests

NORD Webinar Outlines COVID-19 Response on Financial, Policy Fronts

Recovery Is a Long Road Following My Concussion

Surge in Telemedicine One ‘Good’ Outcome from COVID-19 Crisis, Doctors Say

Industry leaders seek to advance innovative resources for rare and orphan disease communities amid COVID-19 outbreak

NORD Opens COVID-19 Financial Aid Program for Rare Disease Community

A Cautionary Tale About Hydroxychloroquine’s Side Effects

Catalyst Pharmaceuticals Confirms Sufficient Supply of Firdapse

LEMS and Exercise

The Importance of Being Mindful During COVID-19

Experts Publish Guidance on Managing MG and LEMS During COVID-19 Pandemic

How to Stay Motivated With a Chronic Disease Like LEMS

Mindfulness for People with LEMS

Catalyst Expects No Supply Problems for Firdapse Due to COVID-19

NORD’s Advice on COVID-19: You’re Stronger Than You Think

NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum

Building Emotional Resilience When You Have LEMS

Timely Treatment Can Be Successful for LEMS Linked to Lung Adenocarcinoma, Case Study Suggests

Pin It on Pinterest