• Rare Diseases Constitute a ‘Public Health Issue,’ NCATS Director Warns
  • Ruzurgi Approved in United States as First Treatment for Children with LEMS
  • SCLC Patients with LEMS Have Better Long-term Survival, Study Suggests
  • LEMS Prevalence in U.S. Similar to Europe, Large U.S. Study Reports
  • Paraneoplastic Cerebellar Degeneration and LEMS Linked to Rare Throat Tumor, Case Report Shows
  • Screening Leads to Simultaneous Lambert–Eaton Myasthenic Syndrome and Limbic Encephalitis Diagnoses, in Unusual Case Report
  • Mouse Model of LEMS Provides New Tool to Develop Therapies
  • Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn
  • Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist
  • NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research
  • Firdapse Found to be Effective for Lambert-Eaton Myasthenic Syndrome, Phase 3 Trial Shows
  • WODC 2019 Organizers Expect 1,200 to Attend Rare Disease Conference in April